Tag: retinal dystrophy


FDA Approves Gene Therapy for Rare Eye Condition

Gene therapy is now a reality. At least in the United States. Today, the U.S. Food and Drug Administration (FDA) approved the gene therapy Luxturna (voretigene neparvovec-rzyl) to treat patients with a rare form of blindness – biallelic RPE65 mutation-associated retinal dystrophy.

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