ERT Delays the Need for a Wheelchair in Pompe Patients (But Not the Need for Respiratory Assistance)
Results from a new survey, published in the OJRD, shows that ERT [Lumizyme (alglucosidase alfa), also known as Myozyme outside of the US] for patients with late-onset Pompe disease significantly reduces the risk of them becoming wheelchair dependent, but did not reduce the need for respiratory assistance.
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