Thanks to a Canadian with a rare disease, Dallas Mavericks owner and Shark Tank Mark Cuban just donated $250,000 towards developing a gene therapy to cure mucopolysacharridosis II (MPS II or Hunter syndrome).
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Whether Kim Angel succeeds at finding that next viral campaign is not known but her patient advocacy group is well organized and ready to accommodate a rapid change in attention and awareness that would come with a viral campaign.
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Shire’s Hunter Syndrome Trial Fails to Meet Primary Endpoint While Advocacy Group Starts its Own Gene Therapy Trial.
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