Tag: hemophilia

Stories

Gene Therapy and Hemophilia A

The results of a phase 1/2, clinical study looking at the safety and efficacy of gene therapy to treat 9 adults with severe hemophilia A was recently published in the New England Journal of Medicine (NEJM). And the results are very promising.

Read More

Gene Therapy and Hemophilia B

This week in the  New England Journal of Medicine, Lindsey George, MD and colleagues report on their Phase 1/2 study assessing the safety and efficacy of gene therapy to treat patients with hemophilia B. And the results are very impressive.

Read More
Loading