Duchenne muscular dystrophy has very limited treatment options and is still a disease that leaves a young boy wheelchair bound. In 1995, Jesse Davidson, a 15-year-old wheelchair bound DMD patient, was pushed by his father, John, across the province of Ontario (3339 kilometers) to raise awareness about the condition.
Read More
Gene therapy for rare diseases continues to make headlines. The latest clinical trial involving gene therapy is one for Duchenne muscular dystrophy (DMD). That trial recently dosed its first patient at the Nationwide Children’s Hospital in Columbus, Ohio.
Read More
In the study, Lingjun Rao Ph.D. and colleagues were able to demonstrate the ability to create functioning human muscle cells out of non-muscle stem cells. The implications could be extraordinary for diseases such as the muscular dystrophies.
Read More
